ENHANCING TRANSDUCTION OF THE LIVER BY ADENO-ASSOCIATED VIRAL VECTORS

od Nathwani, Amit C., Cochrane, Melanie, McIntosh, Jenny, Ng, Catherine Y.C., Zhou, Junfang, Gray, John T., Davidoff, Andrew M.
Wydane 2008

Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman prima...

od Nathwani, Amit C., Gray, John T., McIntosh, Jenny, Ng, Catherine Y. C., Zhou, Junfang, Spence, Yunyu, Cochrane, Melanie, Gray, Elaine, Tuddenham, Edward G. D., Davidoff, Andrew M.
Wydane 2007

Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman...

od Nathwani, Amit C., Gray, John T., Ng, Catherine Y. C., Zhou, Junfang, Spence, Yunyu, Waddington, Simon N., Tuddenham, Edward G. D., Kemball-Cook, Geoffrey, McIntosh, Jenny, Boon-Spijker, Mariette, Mertens, Koen, Davidoff, Andrew M.
Wydane 2006

Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant

od McIntosh, Jenny, Lenting, Peter J., Rosales, Cecilia, Lee, Doyoung, Rabbanian, Samira, Raj, Deepak, Patel, Nishil, Tuddenham, Edward G. D., Christophe, Olivier D., McVey, John H., Waddington, Simon, Nienhuis, Arthur W., Gray, John T., Fagone, Paolo, Mingozzi, Federico, Zhou, Shang-Zhen, High, Katherine A., Cancio, Maria, Ng, Catherine Y. C., Zhou, Junfang, Morton, Christopher L., Davidoff, Andrew M., Nathwani, Amit C.
Wydane 2013

Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

od Nathwani, Amit C., Tuddenham, Edward G.D., Rangarajan, Savita, Rosales, Cecilia, McIntosh, Jenny, Linch, David C., Chowdary, Pratima, Riddell, Anne, Pie, Arnulfo Jaquilmac, Harrington, Chris, O’Beirne, James, Smith, Keith, Pasi, John, Glader, Bertil, Rustagi, Pradip, Ng, Catherine Y.C., Kay, Mark A., Zhou, Junfang, Spence, Yunyu, Morton, Christopher L., Allay, James, Coleman, John, Sleep, Susan, Cunningham, John M., Srivastava, Deokumar, Basner-Tschakarjan, Etiena, Mingozzi, Federico, High, Katherine A., Gray, John T., Reiss, Ulrike M., Nienhuis, Arthur W., Davidoff, Andrew M.
Wydane 2011