Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman primates

Những quyển sách tương tự

• Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman primate liver
  Bằng: Nathwani, Amit C., et al.
  Được phát hành: (2006)
• ENHANCING TRANSDUCTION OF THE LIVER BY ADENO-ASSOCIATED VIRAL VECTORS
  Bằng: Nathwani, Amit C., et al.
  Được phát hành: (2008)
• Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins
  Bằng: Nathwani, Amit C, et al.
  Được phát hành: (2011)
• Strong Cortical and Spinal Cord Transduction After AAV7 and AAV9 Delivery into the Cerebrospinal Fluid of Nonhuman Primates
  Bằng: Samaranch, Lluis, et al.
  Được phát hành: (2013)
• Differential Transduction Following Basal Ganglia Administration of Distinct Pseudotyped AAV Capsid Serotypes in Nonhuman Primates
  Bằng: Dodiya, Hemraj B, et al.
  Được phát hành: (2009)