ENHANCING TRANSDUCTION OF THE LIVER BY ADENO-ASSOCIATED VIRAL VECTORS

Por Nathwani, Amit C., Cochrane, Melanie, McIntosh, Jenny, Ng, Catherine Y.C., Zhou, Junfang, Gray, John T., Davidoff, Andrew M.
Publicado em 2008

Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman prima...

Por Nathwani, Amit C., Gray, John T., McIntosh, Jenny, Ng, Catherine Y. C., Zhou, Junfang, Spence, Yunyu, Cochrane, Melanie, Gray, Elaine, Tuddenham, Edward G. D., Davidoff, Andrew M.
Publicado em 2007

Self-complementary adeno-associated virus vectors containing a novel liver-specific human factor IX expression cassette enable highly efficient transduction of murine and nonhuman...

Por Nathwani, Amit C., Gray, John T., Ng, Catherine Y. C., Zhou, Junfang, Spence, Yunyu, Waddington, Simon N., Tuddenham, Edward G. D., Kemball-Cook, Geoffrey, McIntosh, Jenny, Boon-Spijker, Mariette, Mertens, Koen, Davidoff, Andrew M.
Publicado em 2006

Therapeutic levels of FVIII following a single peripheral vein administration of rAAV vector encoding a novel human factor VIII variant

Por McIntosh, Jenny, Lenting, Peter J., Rosales, Cecilia, Lee, Doyoung, Rabbanian, Samira, Raj, Deepak, Patel, Nishil, Tuddenham, Edward G. D., Christophe, Olivier D., McVey, John H., Waddington, Simon, Nienhuis, Arthur W., Gray, John T., Fagone, Paolo, Mingozzi, Federico, Zhou, Shang-Zhen, High, Katherine A., Cancio, Maria, Ng, Catherine Y. C., Zhou, Junfang, Morton, Christopher L., Davidoff, Andrew M., Nathwani, Amit C.
Publicado em 2013

Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

Por Nathwani, Amit C., Tuddenham, Edward G.D., Rangarajan, Savita, Rosales, Cecilia, McIntosh, Jenny, Linch, David C., Chowdary, Pratima, Riddell, Anne, Pie, Arnulfo Jaquilmac, Harrington, Chris, O’Beirne, James, Smith, Keith, Pasi, John, Glader, Bertil, Rustagi, Pradip, Ng, Catherine Y.C., Kay, Mark A., Zhou, Junfang, Spence, Yunyu, Morton, Christopher L., Allay, James, Coleman, John, Sleep, Susan, Cunningham, John M., Srivastava, Deokumar, Basner-Tschakarjan, Etiena, Mingozzi, Federico, High, Katherine A., Gray, John T., Reiss, Ulrike M., Nienhuis, Arthur W., Davidoff, Andrew M.
Publicado em 2011