Antisense-Oligonucleotide Mediated Exon Skipping in Activin-Receptor-Like Kinase 2: Inhibiting the Receptor That Is Overactive in Fibrodysplasia Ossificans Progressiva

Por Shi, SongTing, Cai, Jie, de Gorter, David J. J., Sanchez-Duffhues, Gonzalo, Kemaladewi, Dwi U., Hoogaars, Willem M. H., Aartsma-Rus, Annemieke, ’t Hoen, Peter A. C., ten Dijke, Peter
Publicado em 2013

Targeting TGF-β Signaling by Antisense Oligonucleotide-mediated Knockdown of TGF-β Type I Receptor

Por Kemaladewi, Dwi U, Pasteuning, Svitlana, van der Meulen, Joke W, van Heiningen, Sandra H, van Ommen, Gert-Jan, ten Dijke, Peter, Aartsma-Rus, Annemieke, ‘t Hoen, Peter AC, Hoogaars, Willem M
Publicado em 2014

Dual exon skipping in myostatin and dystrophin for Duchenne muscular dystrophy

Por Kemaladewi, Dwi U, Hoogaars, Willem MH, van Heiningen, Sandra H, Terlouw, Samuel, de Gorter, David JJ, den Dunnen, Johan T, van Ommen, Gert Jan B, Aartsma-Rus, Annemieke, ten Dijke, Peter, 't Hoen, Peter AC
Publicado em 2011

BMP antagonists enhance myogenic differentiation and ameliorate the dystrophic phenotype in a DMD mouse model

Por Shi, SongTing, Hoogaars, Willem M.H., de Gorter, David J.J., van Heiningen, Sandra H., Lin, Herbert Y., Hong, Charles C., Kemaladewi, Dwi U., Aartsma-Rus, Annemieke, Dijke, Peter ten, ’t Hoen, Peter A.C.
Publicado em 2010

Novel Ex Vivo Culture Method for the Study of Dupuytren's Disease: Effects of TGFβ Type 1 Receptor Modulation by Antisense Oligonucleotides

Por Karkampouna, Sofia, Kruithof, Boudewijn PT, Kloen, Peter, Obdeijn, Miryam C, van der Laan, Annelies MA, Tanke, Hans J, Kemaladewi, Dwi U, Hoogaars, Willem MH, ‘t Hoen, Peter AC, Aartsma-Rus, Annemieke, Clark, Ian M, ten Dijke, Peter, Goumans, Marie-José, Kruithof-de Julio, Marianna
Publicado em 2014

Spell Checking Nature: Versatility of CRISPR/Cas9 for Developing Treatments for Inherited Disorders

Por Wojtal, Daria, Kemaladewi, Dwi U., Malam, Zeenat, Abdullah, Sarah, Wong, Tatianna W.Y., Hyatt, Elzbieta, Baghestani, Zahra, Pereira, Sergio, Stavropoulos, James, Mouly, Vincent, Mamchaoui, Kamel, Muntoni, Francesco, Voit, Thomas, Gonorazky, Hernan D., Dowling, James J., Wilson, Michael D., Mendoza-Londono, Roberto, Ivakine, Evgueni A., Cohn, Ronald D.
Publicado no Am J Hum Genet (2016)