Peptide nucleic acids, morpholinos and related antisense biomolecules

بواسطة Janson, Christopher G., During, Matthew J.
منشور في 2006

Comparison of Endovascular and Intraventricular Gene Therapy With Adeno-Associated Virus–α-L-Iduronidase for Hurler Disease

بواسطة Janson, Christopher G., Romanova, Liudmila G., Leone, Paola, Nan, Zhenhong, Belur, Lalitha, McIvor, R. Scott, Low, Walter C.
منشور في 2014

N-acetylaspartate Supports the Energetic Demands of Developmental Myelination via Oligodendroglial Aspartoacylase

بواسطة Francis, Jeremy S., Wojtas, Ireneusz, Markov, Vladimir, Gray, Steven J., McCown, Thomas J., Samulski, R. Jude, Bilaniuk, Larissa T., Wang, Dah-Jyuu, De Vivo, Darryl C., Janson, Christopher G., Leone, Paola
الحاوية / القاعدة Neurobiol Dis (2016)

Long-Term Follow-Up After Gene Therapy for Canavan Disease

بواسطة Leone, Paola, Shera, David, McPhee, Scott W.J., Francis, Jeremy S., Kolodny, Edwin H., Bilaniuk, Larissa T., Wang, Dah-Jyuu, Assadi, Mitra, Goldfarb, Olga, Goldman, H. Warren, Freese, Andrew, Young, Deborah, During, Matthew J., Samulski, R. Jude, Janson, Christopher G.
منشور في 2012