Gene Therapy for Retinitis Pigmentosa Caused by MFRP Mutations: Human Phenotype and Preliminary Proof of Concept

Por Dinculescu, Astra, Estreicher, Jackie, Zenteno, Juan C., Aleman, Tomas S., Schwartz, Sharon B., Huang, Wei Chieh, Roman, Alejandro J., Sumaroka, Alexander, Li, Qiuhong, Deng, Wen-Tao, Min, Seok-Hong, Chiodo, Vince A., Neeley, Andy, Liu, Xuan, Shu, Xinhua, Matias-Florentino, Margarita, Buentello-Volante, Beatriz, Boye, Sanford L., Cideciyan, Artur V., Hauswirth, William W., Jacobson, Samuel G.
Publicado em 2011