RNA-Seq Analysis of an Antisense Sequence Optimized for Exon Skipping in Duchenne Patients Reveals No Off-Target Effect

od Domenger, Claire, Allais, Marine, François, Virginie, Léger, Adrien, Lecomte, Emilie, Montus, Marie, Servais, Laurent, Voit, Thomas, Moullier, Philippe, Audic, Yann, Le Guiner, Caroline
Wydane w Mol Ther Nucleic Acids (2017)

Cell-specific CRISPR–Cas9 activation by microRNA-dependent expression of anti-CRISPR proteins

od Hoffmann, Mareike D, Aschenbrenner, Sabine, Grosse, Stefanie, Rapti, Kleopatra, Domenger, Claire, Fakhiri, Julia, Mastel, Manuel, Börner, Kathleen, Eils, Roland, Grimm, Dirk, Niopek, Dominik
Wydane w Nucleic Acids Res (2019)

Forelimb Treatment in a Large Cohort of Dystrophic Dogs Supports Delivery of a Recombinant AAV for Exon Skipping in Duchenne Patients

od Le Guiner, Caroline, Montus, Marie, Servais, Laurent, Cherel, Yan, Francois, Virginie, Thibaud, Jean-Laurent, Wary, Claire, Matot, Béatrice, Larcher, Thibaut, Guigand, Lydie, Dutilleul, Maeva, Domenger, Claire, Allais, Marine, Beuvin, Maud, Moraux, Amélie, Le Duff, Johanne, Devaux, Marie, Jaulin, Nicolas, Guilbaud, Mickaël, Latournerie, Virginie, Veron, Philippe, Boutin, Sylvie, Leborgne, Christian, Desgue, Diana, Deschamps, Jack-Yves, Moullec, Sophie, Fromes, Yves, Vulin, Adeline, Smith, Richard H, Laroudie, Nicolas, Barnay-Toutain, Frédéric, Rivière, Christel, Bucher, Stéphanie, Le, Thanh-Hoa, Delaunay, Nicolas, Gasmi, Mehdi, Kotin, Robert M, Bonne, Gisèle, Adjali, Oumeya, Masurier, Carole, Hogrel, Jean-Yves, Carlier, Pierre, Moullier, Philippe, Voit, Thomas
Wydane w Mol Ther (2014)