A scalable method for the production of high-titer and high-quality adeno-associated type 9 vectors using the HSV platform

af Adamson-Small, Laura, Potter, Mark, Falk, Darin J, Cleaver, Brian, Byrne, Barry J, Clément, Nathalie
Udgivet i Mol Ther Methods Clin Dev (2016)

IT-35 cGMP MANUFACTURING OF EX VIVO EXPANDED TUMOR-SPECIFIC T CELLS AND AMPLIFIED TUMOR RNA-PULSED DC VACCINES TARGETING GLIOBLASTOMA AND MEDULLOBLASTOMA

af Yegorov, Oleg, Dechkovskaia, Anjelika, Drake, Jeffery, Cleaver, Brian D., Clement, Nathalie, Huang, Jianping, Mitchell, Duane A.
Udgivet 2014

PDCT-08. TRACKING THE T CELL REPERTOIRE AFTER ADOPTIVE CELL THERAPY IN PEDIATRIC PATIENTS WITH RECURRENT MEDULLOBLASTOMA

af Yegorov, Oleg, Yegorova, Yanina, Dechkovskaia, Anjelika, Cleaver, Brian, Clement, Nathalie, Slayton, William, Gururangan, Sridharan, Mitchell, Duane
Udgivet i Neuro Oncol (2018)

ATIM-34. SINGLE-CELL RNA SEQUENCING REVEALS DYNAMIC IMMUNE RESPONSE CHANGES IN GLIOBLASTOMA PATIENT WITH DURABLE COMPLETE RESPONSE TO CMV PP65-LAMP RNA-PULSED DENDRITIC VACCINES

af Yegorov, Oleg, Yang, Changlin, Rahman, Maryam, Ghiaseddin, Ashley, Dechkovskaia, Anjelika, Cleaver, Brian, Hodik, Marcia, Amdur, Robert, Massini, Tara, Kresak, Jesse, Mitchell, Duane
Udgivet i Neuro Oncol (2019)

Pompe disease gene therapy: neural manifestations require consideration of CNS directed therapy

af Byrne, Barry J., Fuller, David D., Smith, Barbara K., Clement, Nathalie, Coleman, Kirsten, Cleaver, Brian, Vaught, Lauren, Falk, Darin J., McCall, Angela, Corti, Manuela
Udgivet i Ann Transl Med (2019)

A simplified purification protocol for recombinant adeno-associated virus vectors

af Potter, Mark, Lins, Bridget, Mietzsch, Mario, Heilbronn, Regine, Van Vliet, Kim, Chipman, Paul, Agbandje-McKenna, Mavis, Cleaver, Brian D, Clément, Nathalie, Byrne, Barry J, Zolotukhin, Sergei
Udgivet i Mol Ther Methods Clin Dev (2014)

Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning

af Corti, Manuela, Cleaver, Brian, Clément, Nathalie, Conlon, Thomas J., Faris, Kaitlyn J., Wang, Gensheng, Benson, Janet, Tarantal, Alice F., Fuller, Davis, Herzog, Roland W., Byrne, Barry J.
Udgivet i Hum Gene Ther Clin Dev (2015)

Phase I/II Trial of Adeno-Associated Virus–Mediated Alpha-Glucosidase Gene Therapy to the Diaphragm for Chronic Respiratory Failure in Pompe Disease: Initial Safety and Ventilatory...

af Smith, Barbara K., Collins, Shelley W., Conlon, Thomas J., Mah, Cathryn S., Lawson, Lee Ann, Martin, Anatole D., Fuller, David D., Cleaver, Brian D., Clément, Nathalie, Phillips, Dawn, Islam, Saleem, Dobjia, Nicole, Byrne, Barry J.
Udgivet 2013

Preclinical Potency and Safety Studies of an AAV2-Mediated Gene Therapy Vector for the Treatment of MERTK Associated Retinitis Pigmentosa

af Conlon, Thomas J., Deng, Wen-Tao, Erger, Kirsten, Cossette, Travis, Pang, Ji-jing, Ryals, Renee, Clément, Nathalie, Cleaver, Brian, McDoom, Issam, Boye, Shannon E., Peden, Marc C., Sherwood, Mark B., Abernathy, Corinne R., Alkuraya, Fowzan S., Boye, Sanford L., Hauswirth, William W.
Udgivet 2013

Pompe disease gene therapy

af Byrne, Barry J., Falk, Darin J., Pacak, Christina A., Nayak, Sushrusha, Herzog, Roland W., Elder, Melissa E., Collins, Shelley W., Conlon, Thomas J., Clement, Nathalie, Cleaver, Brian D., Cloutier, Denise A., Porvasnik, Stacy L., Islam, Saleem, Elmallah, Mai K., Martin, Anatole, Smith, Barbara K., Fuller, David D., Lawson, Lee Ann, Mah, Cathryn S.
Udgivet 2011