New therapeutic targets in transfusion-dependent and -independent thalassemia

Tekijä Cappellini, M. Domenica, Motta, Irene
Julkaisussa Hematology Am Soc Hematol Educ Program (2017)

Coagulopathy in Beta-Thalassemia: Current Understanding and Future Perspectives

Tekijä Cappellini, M. Domenica, Musallam, Khaled M., Marcon, Alessia, Taher, Ali T.
Julkaistu 2009

Treating iron overload in patients with non-transfusion-dependent thalassemia

Tekijä Taher, Ali T, Viprakasit, Vip, Musallam, Khaled M, Cappellini, M Domenica
Julkaistu 2013

Efficacy and safety of iron-chelation therapy with deferoxamine, deferiprone, and deferasirox for the treatment of iron-loaded patients with nontransfusion-dependent thalassemia sy...

Tekijä Taher, Ali T, Porter, John B, Kattamis, Antonis, Viprakasit, Vip, Cappellini, M Domenica
Julkaisussa Drug Des Devel Ther (2016)

Approaching low liver iron burden in chelated patients with non-transfusion-dependent thalassemia: the safety profile of deferasirox

Tekijä Taher, Ali T, Porter, John B, Viprakasit, Vip, Kattamis, Antonis, Chuncharunee, Suporn, Sutcharitchan, Pranee, Siritanaratkul, Noppadol, Origa, Raffaella, Karakas, Zeynep, Habr, Dany, Zhu, Zewen, Cappellini, M Domenica
Julkaisussa Eur J Haematol (2014)

Deferasirox demonstrates a dose-dependent reduction in liver iron concentration and consistent efficacy across subgroups of non-transfusion-dependent thalassemia patients

Tekijä Taher, Ali T, Porter, John B, Viprakasit, Vip, Kattamis, Antonis, Chuncharunee, Suporn, Sutcharitchan, Pranee, Siritanaratkul, Noppadol, Galanello, Renzo, Karakas, Zeynep, Lawniczek, Tomasz, Habr, Dany, Ros, Jacqueline, Zhang, Yiyun, Cappellini, M Domenica
Julkaistu 2013

Deferasirox effectively reduces iron overload in non-transfusion-dependent thalassemia (NTDT) patients: 1-year extension results from the THALASSA study

Tekijä Taher, Ali T., Porter, John B., Viprakasit, Vip, Kattamis, Antonis, Chuncharunee, Suporn, Sutcharitchan, Pranee, Siritanaratkul, Noppadol, Galanello, Renzo, Karakas, Zeynep, Lawniczek, Tomasz, Habr, Dany, Ros, Jacqueline, Zhu, Zewen, Cappellini, M. Domenica
Julkaistu 2013

Effects of deferasirox-deferoxamine on myocardial and liver iron in patients with severe transfusional iron overload

Tekijä Aydinok, Yesim, Kattamis, Antonis, Cappellini, M. Domenica, El-Beshlawy, Amal, Origa, Raffaella, Elalfy, Mohsen, Kilinç, Yurdanur, Perrotta, Silverio, Karakas, Zeynep, Viprakasit, Vip, Habr, Dany, Constantinovici, Niculae, Shen, Junwu, Porter, John B.
Julkaisussa Blood (2015)

The autophagy-activating kinase ULK1 mediates clearance of free α-globin in β-thalassemia

Tekijä Lechauve, Christophe, Keith, Julia, Khandros, Eugene, Fowler, Stephanie, Mayberry, Kalin, Freiwan, Abdullah, Thom, Christopher S., Delbini, Paola, Romero, Emilio Boada, Zhang, Jingjing, Motta, Irene, Tillman, Heather, Cappellini, M. Domenica, Kundu, Mondira, Weiss, Mitchell J.
Julkaisussa Sci Transl Med (2019)

Decreased differentiation of erythroid cells exacerbates ineffective erythropoiesis in β-thalassemia

Tekijä Libani, Ilaria V., Guy, Ella C., Melchiori, Luca, Schiro, Raffaella, Ramos, Pedro, Breda, Laura, Scholzen, Thomas, Chadburn, Amy, Liu, YiFang, Kernbach, Margrit, Baron-Lühr, Bettina, Porotto, Matteo, de Sousa, Maria, Rachmilewitz, Eliezer A., Hood, John D., Cappellini, M. Domenica, Giardina, Patricia J., Grady, Robert W., Gerdes, Johannes, Rivella, Stefano
Julkaistu 2008