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The infantile-onset form of Pompe disease: an autopsy diagnosis

Pompe disease (PD) is a rare, inherited autosomal recessive metabolic disorder caused by the deficiency of the lysosomal acid alpha-glucosidase (GAA) enzyme described in 1932 by the Dutch pathologist Joannes Cassianus Pompe. The prevalence of PD ranges from 1:40,000 to 1:300,000 births and depends o...

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Bibliografske podrobnosti
izdano v:Autopsy and Case Reports
Main Authors: Otávio César Cruz dos Santos, Regina Schultz
Format: Artigo
Jezik:Inglês
Izdano: Hospital Universitário da Universidade de São Paulo 2015
Teme:
Online dostop:https://www.redalyc.org/articulo.oa?id=576060831008
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