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The infantile-onset form of Pompe disease: an autopsy diagnosis

Pompe disease (PD) is a rare, inherited autosomal recessive metabolic disorder caused by the deficiency of the lysosomal acid alpha-glucosidase (GAA) enzyme described in 1932 by the Dutch pathologist Joannes Cassianus Pompe. The prevalence of PD ranges from 1:40,000 to 1:300,000 births and depends o...

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Dettagli Bibliografici
Pubblicato in:Autops Case Rep
Autori principali: dos Santos, Otávio César Cruz, Schultz, Regina
Natura: Artigo
Lingua:Inglês
Pubblicazione: São Paulo, SP: Universidade de São Paulo, Hospital Universitário 2015
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4757919/
https://ncbi.nlm.nih.gov/pubmed/26894045
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4322/acr.2015.022
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