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The future of retinal gene therapy: evolving from subretinal to intravitreal vector delivery
Inherited retinal degenerations are a leading and untreatbale cause of blindness, and as such they are targets for gene therapy. Numerous gene therapy treatments have progressed from laboratory research to clinical trails, and a pioneering gene therapy received the first ever FDA approval for treati...
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| Опубликовано в: : | Neural Regen Res |
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| Главные авторы: | , |
| Формат: | Artigo |
| Язык: | Inglês |
| Опубликовано: |
Wolters Kluwer - Medknow
2021
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| Предметы: | |
| Online-ссылка: | https://ncbi.nlm.nih.gov/pmc/articles/PMC8328774/ https://ncbi.nlm.nih.gov/pubmed/33510064 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4103/1673-5374.306063 |
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