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Spinal muscular atrophy: From approved therapies to future therapeutic targets for personalized medicine

Spinal muscular atrophy (SMA) is a devastating childhood motor neuron disease that, in the most severe cases and when left untreated, leads to death within the first two years of life. Recent therapeutic advances have given hope to families and patients by compensating for the deficiency in survival...

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Foilsithe in:Cell Rep Med
Main Authors: Chaytow, Helena, Faller, Kiterie M.E., Huang, Yu-Ting, Gillingwater, Thomas H.
Formáid: Artigo
Teanga:Inglês
Foilsithe: Elsevier 2021
Ábhair:
Rochtain Ar Líne:https://ncbi.nlm.nih.gov/pmc/articles/PMC8324491/
https://ncbi.nlm.nih.gov/pubmed/34337562
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.xcrm.2021.100346
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