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Clinical Perspectives of Gene-Targeted Therapies for Epidermolysis Bullosa

New insights into molecular genetics and pathomechanisms in epidermolysis bullosa (EB), methodological and technological advances in molecular biology as well as designated funding initiatives and facilitated approval procedures for orphan drugs have boosted translational research perspectives for t...

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Dettagli Bibliografici
Pubblicato in:Dermatol Ther (Heidelb)
Autori principali: Welponer, Tobias, Prodinger, Christine, Pinon-Hofbauer, Josefina, Hintersteininger, Arno, Breitenbach-Koller, Hannelore, Bauer, Johann W., Laimer, Martin
Natura: Artigo
Lingua:Inglês
Pubblicazione: Springer Healthcare 2021
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC8322229/
https://ncbi.nlm.nih.gov/pubmed/34110606
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s13555-021-00561-5
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