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Measuring health-related quality of life in patients with rare disease

BACKGROUND: There has been a growing emphasis on health-related quality of life (HRQoL) as an important outcome in rare disease drug development, although its assessment may be useful outside the drug development context, including in clinical applications or natural history studies. Central to asse...

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Dades bibliogràfiques
Publicat a:J Patient Rep Outcomes
Autors principals: Lenderking, William R., Anatchkova, Milena, Pokrzywinski, Robin, Skalicky, Anne, Martin, Mona L., Gelhorn, Heather
Format: Artigo
Idioma:Inglês
Publicat: Springer International Publishing 2021
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC8292508/
https://ncbi.nlm.nih.gov/pubmed/34283357
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s41687-021-00336-8
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