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New Therapies to Correct the Cystic Fibrosis Basic Defect
Rare diseases affect 400 million individuals worldwide and cause significant morbidity and mortality. Finding solutions for rare diseases can be very challenging for physicians and researchers. Cystic fibrosis (CF), a genetic, autosomal recessive, multisystemic, life-limiting disease does not escape...
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| Publicado no: | Int J Mol Sci |
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| Main Authors: | , |
| Formato: | Artigo |
| Idioma: | Inglês |
| Publicado em: |
MDPI
2021
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| Assuntos: | |
| Acesso em linha: | https://ncbi.nlm.nih.gov/pmc/articles/PMC8227161/ https://ncbi.nlm.nih.gov/pubmed/34201249 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms22126193 |
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