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New Therapies to Correct the Cystic Fibrosis Basic Defect

Rare diseases affect 400 million individuals worldwide and cause significant morbidity and mortality. Finding solutions for rare diseases can be very challenging for physicians and researchers. Cystic fibrosis (CF), a genetic, autosomal recessive, multisystemic, life-limiting disease does not escape...

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Detalles Bibliográficos
Publicado en:Int J Mol Sci
Main Authors: Bergeron, Christelle, Cantin, André M.
Formato: Artigo
Idioma:Inglês
Publicado: MDPI 2021
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC8227161/
https://ncbi.nlm.nih.gov/pubmed/34201249
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms22126193
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