An Engineered sgsh Mutant Zebrafish Recapitulates Molecular and Behavioural Pathobiology of Sanfilippo Syndrome A/MPS IIIA

Những quyển sách tương tự

• Mutational analysis of Sanfilippo syndrome type A (MPS IIIA): identification of 13 novel mutations
  Bằng: BEESLEY, C., et al.
  Được phát hành: (2000)
• AAVrh10 Vector Corrects Disease Pathology in MPS IIIA Mice and Achieves Widespread Distribution of SGSH in Large Animal Brains
  Bằng: Michaël Hocquemiller, et al.
  Được phát hành: (2020-06-01)
• AAVrh10 Vector Corrects Disease Pathology in MPS IIIA Mice and Achieves Widespread Distribution of SGSH in Large Animal Brains
  Bằng: Hocquemiller, Michaël, et al.
  Được phát hành: (2019)
• Broad Functional Correction of Molecular Impairments by Systemic Delivery of scAAVrh74-hSGSH Gene Delivery in MPS IIIA Mice
  Bằng: Duncan, F Jason, et al.
  Được phát hành: (2015)
• Functional correction of neurological and somatic disorders at later stages of disease in MPS IIIA mice by systemic scAAV9-hSGSH gene delivery
  Bằng: Fu, Haiyan, et al.
  Được phát hành: (2016)