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Promising therapeutic approaches using CRISPR/Cas9 genome editing technology in the treatment of Duchenne muscular dystrophy

Duchenne muscular dystrophy is an X-linked recessive hereditary monogenic disorder caused by inability to produce dystrophin protein. In most patients, the expression of dystrophin lost due to disrupting mutations in open reading frame. Despite the efforts in a large number of different therapeutic...

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Detalles Bibliográficos
Publicado en:Genes Dis
Main Authors: Mollanoori, Hasan, Rahmati, Yazdan, Hassani, Bita, Havasi Mehr, Meysam, Teimourian, Shahram
Formato: Artigo
Idioma:Inglês
Publicado: Chongqing Medical University 2020
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC8099695/
https://ncbi.nlm.nih.gov/pubmed/33997161
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.gendis.2019.12.007
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