Carregant...

Promising therapeutic approaches using CRISPR/Cas9 genome editing technology in the treatment of Duchenne muscular dystrophy

Duchenne muscular dystrophy is an X-linked recessive hereditary monogenic disorder caused by inability to produce dystrophin protein. In most patients, the expression of dystrophin lost due to disrupting mutations in open reading frame. Despite the efforts in a large number of different therapeutic...

Descripció completa

Guardat en:
Dades bibliogràfiques
Publicat a:Genes Dis
Autors principals: Mollanoori, Hasan, Rahmati, Yazdan, Hassani, Bita, Havasi Mehr, Meysam, Teimourian, Shahram
Format: Artigo
Idioma:Inglês
Publicat: Chongqing Medical University 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC8099695/
https://ncbi.nlm.nih.gov/pubmed/33997161
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.gendis.2019.12.007
Etiquetes: Afegir etiqueta
Sense etiquetes, Sigues el primer a etiquetar aquest registre!