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Recent Advances in Elucidating Niemann‐Pick C Disease

Lysosomal sequestration of endocytosed LDL‐derived cholesterol, premature and abnormal enrichment of cholesterol in trans Golgi cisternae and accompanying anomalies in intracellular sterol trafficking are the hallmark phenotypic features of the Niemann‐Pick C (NPC) lesion. A variable severity of the...

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Detalles Bibliográficos
Publicado en:Brain Pathol
Autores principales: Vanier, Marie T., Suzuki, Kinuko
Formato: Artigo
Lenguaje:Inglês
Publicado: Blackwell Publishing Ltd 2006
Materias:
Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC8098395/
https://ncbi.nlm.nih.gov/pubmed/9458174
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/j.1750-3639.1998.tb00143.x
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