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Human recombinant lysosomal β-Hexosaminidases produced in Pichia pastoris efficiently reduced lipid accumulation in Tay-Sachs fibroblasts

GM2 gangliosidosis, Tay-Sachs and Sandhoff diseases, are lysosomal storage disorders characterized by the lysosomal accumulation of GM2 gangliosides. This accumulation is due to deficiency in the activity of the β-hexosaminidases Hex-A or Hex-B, which are dimeric hydrolases formed by αβ or ββ subuni...

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Detalles Bibliográficos
Publicado en:Am J Med Genet C Semin Med Genet
Main Authors: Espejo-Mojica, Angela J., Rodríguez-López, Alexander, Li, Rong, Zheng, Wei, Alméciga-Díaz, Carlos J., Dulcey-Sepúlveda, Cindy, Combariza, Germán, Barrera, Luis A.
Formato: Artigo
Idioma:Inglês
Publicado: 2020
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC8045741/
https://ncbi.nlm.nih.gov/pubmed/33111489
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/ajmg.c.31849
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