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Carrier frequency and incidence estimation of Smith–Lemli–Opitz syndrome in East Asian populations by Genome Aggregation Database (gnomAD) based analysis

BACKGROUND: Smith–Lemli–Opitz syndrome (SLOS) is an autosomal, recessively inherited congenital malformation syndrome characterized by multiple congenital anomalies such as microcephaly with mental defects, distinctive facial features, genital abnormalities, and 2–3 syndactyly of the toes. SLOS is c...

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Détails bibliographiques
Publié dans:Orphanet J Rare Dis
Auteurs principaux: Park, Jong Eun, Lee, Taeheon, Ha, Kyeongsu, Ki, Chang-Seok
Format: Artigo
Langue:Inglês
Publié: BioMed Central 2021
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC8033735/
https://ncbi.nlm.nih.gov/pubmed/33836803
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-021-01789-2
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