Загрузка...
Long-term neurodevelopmental outcomes of hematopoietic stem cell transplantation for late-infantile Krabbe disease
Krabbe disease is a rare neurodegenerative disorder caused by a deficiency in galactocerebrosidase. The only effective treatment is hematopoietic stem cell transplantation (HSCT). Approximately 85% of Krabbe disease cases are the infantile subtypes, among which ∼20% are late infantile. Prior studies...
Сохранить в:
| Опубликовано в: : | Blood |
|---|---|
| Главные авторы: | , , , , |
| Формат: | Artigo |
| Язык: | Inglês |
| Опубликовано: |
American Society of Hematology
2021
|
| Предметы: | |
| Online-ссылка: | https://ncbi.nlm.nih.gov/pmc/articles/PMC8020262/ https://ncbi.nlm.nih.gov/pubmed/33150395 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/blood.2020005477 |
| Метки: |
Добавить метку
Нет меток, Требуется 1-ая метка записи!
|