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Recombinant VWF fragments improve bioavailability of subcutaneous factor VIII in hemophilia A mice

Conventional treatment of hemophilia A (HA) requires repetitive IV injection of coagulation factor VIII (FVIII). Subcutaneous administration of FVIII is inefficient because of binding to the extravascular matrix, in particular to phospholipids (PLs), and subsequent proteolysis. To overcome this, rec...

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Detalles Bibliográficos
Publicado en:Blood
Main Authors: Vollack-Hesse, Nadine, Oleshko, Olga, Werwitzke, Sonja, Solecka-Witulska, Barbara, Kannicht, Christoph, Tiede, Andreas
Formato: Artigo
Idioma:Inglês
Publicado: American Society of Hematology 2021
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC7952839/
https://ncbi.nlm.nih.gov/pubmed/32877516
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/blood.2020006468
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