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HLA-haploidentical TCRαβ(+)/CD19(+)-depleted stem cell transplantation in children and young adults with Fanconi anemia

We report on the outcome of 24 patients with Fanconi anemia (FA) lacking an HLA matched related or unrelated donor, given an HLA-haploidentical T-cell receptor αβ (TCRαβ(+)) and CD19(+) cell-depleted hematopoietic stem cell transplantation (HSCT) in the context of a prospective, single-center phase...

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Dades bibliogràfiques
Publicat a:Blood Adv
Autors principals: Strocchio, Luisa, Pagliara, Daria, Algeri, Mattia, Li Pira, Giuseppina, Rossi, Francesca, Bertaina, Valentina, Leone, Giovanna, Pinto, Rita Maria, Andreani, Marco, Agolini, Emanuele, Girardi, Katia, Gaspari, Stefania, Grapulin, Lavinia, del Bufalo, Francesca, Novelli, Antonio, Merli, Pietro, Locatelli, Franco
Format: Artigo
Idioma:Inglês
Publicat: American Society of Hematology 2021
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7948273/
https://ncbi.nlm.nih.gov/pubmed/33656536
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/bloodadvances.2020003707
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