Načítá se...

Dystrophin Gene-Editing Stability Is Dependent on Dystrophin Levels in Skeletal but Not Cardiac Muscles

Gene editing is often touted as a permanent method for correcting mutations, but its long-term benefits in Duchenne muscular dystrophy (DMD) may depend on sufficiently high editing efficiencies to halt muscle degeneration. Here, we explored the persistence of dystrophin expression following recombin...

Celý popis

Uloženo v:
Podrobná bibliografie
Vydáno v:Mol Ther
Hlavní autoři: Bengtsson, Niclas E., Tasfaout, Hichem, Hauschka, Stephen D., Chamberlain, Jeffrey S.
Médium: Artigo
Jazyk:Inglês
Vydáno: American Society of Gene & Cell Therapy 2021
Témata:
On-line přístup:https://ncbi.nlm.nih.gov/pmc/articles/PMC7934576/
https://ncbi.nlm.nih.gov/pubmed/33160075
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymthe.2020.11.003
Tagy: Přidat tag
Žádné tagy, Buďte první, kdo otaguje tento záznam!