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In vivo Genome Editing Therapeutic Approaches for Neurological Disorders: Where Are We in the Translational Pipeline?

In vivo genome editing tools, such as those based on CRISPR, have been increasingly utilized in both basic and translational neuroscience research. There are currently nine in vivo non-CNS genome editing therapies in clinical trials, and the pre-clinical pipeline of major biotechnology companies dem...

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Detalhes bibliográficos
Publicado no:Front Neurosci
Main Authors: Lubroth, Pablo, Colasante, Gaia, Lignani, Gabriele
Formato: Artigo
Idioma:Inglês
Publicado em: Frontiers Media S.A. 2021
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7930815/
https://ncbi.nlm.nih.gov/pubmed/33679313
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fnins.2021.632522
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