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Decision-Making And Selection Bias in Four Observational Studies on Duchenne and Becker Muscular Dystrophy
BACKGROUND: Natural history data are essential for trial design in Duchenne (DMD) and Becker muscular dystrophy (BMD), but recruitment for observational studies can be challenging. OBJECTIVE: We reviewed reasons why patients or caregivers declined participation, and compared characteristics of parti...
Gorde:
| Argitaratua izan da: | J Neuromuscul Dis |
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| Egile Nagusiak: | , , , , , , , , , |
| Formatua: | Artigo |
| Hizkuntza: | Inglês |
| Argitaratua: |
IOS Press
2020
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| Gaiak: | |
| Sarrera elektronikoa: | https://ncbi.nlm.nih.gov/pmc/articles/PMC7902964/ https://ncbi.nlm.nih.gov/pubmed/32925089 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3233/JND-200541 |
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