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Decision-Making And Selection Bias in Four Observational Studies on Duchenne and Becker Muscular Dystrophy

BACKGROUND: Natural history data are essential for trial design in Duchenne (DMD) and Becker muscular dystrophy (BMD), but recruitment for observational studies can be challenging. OBJECTIVE: We reviewed reasons why patients or caregivers declined participation, and compared characteristics of parti...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:J Neuromuscul Dis
Egile Nagusiak: Naarding, Karin J., Doorenweerd, Nathalie, Koeks, Zaïda, Hendriksen, Ruben G.F., Chotkan, Kinita A., Krom, Yvonne D., de Groot, Imelda J.M., Straathof, Chiara S., Niks, Erik H., Kan, Hermien E.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: IOS Press 2020
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC7902964/
https://ncbi.nlm.nih.gov/pubmed/32925089
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3233/JND-200541
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