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Developments in evidence creation for treatments of inborn errors of metabolism

Inborn errors of metabolism (IEM) represent the first group of genetic disorders, amenable to causal therapies. In addition to traditional medical diet and cofactor treatments, new treatment strategies such as enzyme replacement and small molecule therapies, solid organ transplantation, and cell‐and...

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Detalhes bibliográficos
Publicado no:J Inherit Metab Dis
Main Authors: Stockler‐Ipsiroglu, Sylvia, Potter, Beth K., Yuskiv, Nataliya, Tingley, Kylie, Patterson, Marc, van Karnebeek, Clara
Formato: Artigo
Idioma:Inglês
Publicado em: John Wiley & Sons, Inc. 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7891579/
https://ncbi.nlm.nih.gov/pubmed/32944978
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/jimd.12315
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