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Shared ACVR1 mutations in FOP and DIPG: Opportunities and challenges in extending biological and clinical implications across rare diseases

Gain-of-function mutations in the Type I Bone Morphogenic Protein (BMP) receptor ACVR1 have been identified in two diseases: Fibrodysplasia Ossificans Progressiva (FOP), a rare autosomal dominant disorder characterized by genetically driven heterotopic ossification, and in 20–25% of diffuse intrinsi...

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Detalhes bibliográficos
Publicado no:Bone
Main Authors: Han, Harry J, Jain, Payal, Resnick, Adam C.
Formato: Artigo
Idioma:Inglês
Publicado em: 2017
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7888549/
https://ncbi.nlm.nih.gov/pubmed/28780023
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.bone.2017.08.001
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