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Long-term health-related quality of life in patients treated with subcutaneous C1-inhibitor replacement therapy for the prevention of hereditary angioedema attacks: findings from the COMPACT open-label extension study

BACKGROUND: Long-term prophylaxis with subcutaneous C1-inhibitor (C1-INH[SC]; HAEGARDA, CSL Behring) in patients with hereditary angioedema (HAE) due to C1-INH deficiency (C1-INH-HAE) was evaluated in an open-label extension follow-up study to the international, double-blind, placebo-controlled COMP...

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Xehetasun bibliografikoak
Argitaratua izan da:Orphanet J Rare Dis
Egile Nagusiak: Lumry, William R., Zuraw, Bruce, Cicardi, Marco, Craig, Timothy, Anderson, John, Banerji, Aleena, Bernstein, Jonathan A., Caballero, Teresa, Farkas, Henriette, Gower, Richard G., Keith, Paul K., Levy, Donald S., Li, H. Henry, Magerl, Markus, Manning, Michael, Riedl, Marc A., Lawo, John-Philip, Prusty, Subhransu, Machnig, Thomas, Longhurst, Hilary
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: BioMed Central 2021
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC7885603/
https://ncbi.nlm.nih.gov/pubmed/33588897
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s13023-020-01658-4
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