A carregar...

A Genotype-Phenotype Correlation Study of Exon Skip-Equivalent In-Frame Deletions and Exon Skip-Amenable Out-of-Frame Deletions across the DMD Gene to Simulate the Effects of Exon-Skipping Therapies: A Meta-Analysis

Dystrophinopathies are caused by mutations in the DMD gene. Out-of-frame deletions represent most mutational events in severe Duchenne muscular dystrophy (DMD), while in-frame deletions typically lead to milder Becker muscular dystrophy (BMD). Antisense oligonucleotide-mediated exon skipping convert...

ver descrição completa

Na minha lista:
Detalhes bibliográficos
Publicado no:J Pers Med
Main Authors: Anwar, Saeed, He, Merry, Lim, Kenji Rowel Q., Maruyama, Rika, Yokota, Toshifumi
Formato: Artigo
Idioma:Inglês
Publicado em: MDPI 2021
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7830903/
https://ncbi.nlm.nih.gov/pubmed/33466756
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/jpm11010046
Tags: Adicionar Tag
Sem tags, seja o primeiro a adicionar uma tag!