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Visual System Impairment in a Mouse Model of Krabbe Disease: The Twitcher Mouse

Krabbe disease (KD, or globoid cell leukodystrophy; OMIM #245200) is an inherited neurodegenerative condition belonging to the class of the lysosomal storage disorders. It is caused by genetic alterations in the gene encoding for the enzyme galactosylceramidase, which is responsible for cleaving the...

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Dettagli Bibliografici
Pubblicato in:Biomolecules
Autori principali: Tonazzini, Ilaria, Cerri, Chiara, Del Grosso, Ambra, Antonini, Sara, Allegra, Manuela, Caleo, Matteo, Cecchini, Marco
Natura: Artigo
Lingua:Inglês
Pubblicazione: MDPI 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7824544/
https://ncbi.nlm.nih.gov/pubmed/33374753
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/biom11010007
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