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Overcoming innate immune barriers that impede AAV gene therapy vectors

The field of gene therapy has made considerable progress over the past several years. Adeno-associated virus (AAV) vectors have emerged as promising and attractive tools for in vivo gene therapy. Despite the recent clinical successes achieved with recombinant AAVs (rAAVs) for therapeutics, host immu...

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Dettagli Bibliografici
Pubblicato in:J Clin Invest
Autori principali: Muhuri, Manish, Maeda, Yukiko, Ma, Hong, Ram, Sanjay, Fitzgerald, Katherine A., Tai, Phillip W.L., Gao, Guangping
Natura: Artigo
Lingua:Inglês
Pubblicazione: American Society for Clinical Investigation 2021
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7773343/
https://ncbi.nlm.nih.gov/pubmed/33393506
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI143780
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