Загрузка...
Short-duration splice promoting compound enables a tunable mouse model of spinal muscular atrophy
Spinal muscular atrophy (SMA) is a motor neuron disease and the leading genetic cause of infant mortality. SMA results from insufficient survival motor neuron (SMN) protein due to alternative splicing. Antisense oligonucleotides, gene therapy and splicing modifiers recently received FDA approval. Al...
Сохранить в:
| Опубликовано в: : | Life Sci Alliance |
|---|---|
| Главные авторы: | , , , , , , |
| Формат: | Artigo |
| Язык: | Inglês |
| Опубликовано: |
Life Science Alliance LLC
2020
|
| Предметы: | |
| Online-ссылка: | https://ncbi.nlm.nih.gov/pmc/articles/PMC7723287/ https://ncbi.nlm.nih.gov/pubmed/33234679 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.26508/lsa.202000889 |
| Метки: |
Добавить метку
Нет меток, Требуется 1-ая метка записи!
|