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A simple Rx for congenital erythropoietic porphyria

In this issue of Blood, Blouin et al(1) describe studies in a murine model of congenital erythropoietic porphyria (CEP). They treated CEP mice for 26 weeks with deferiprone (an iron chelator) and report that it reversed their skin photosensitivity and hemolytic anemia. The murine model closely mirro...

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Detalles Bibliográficos
Publicado en:Blood
Autor Principal: Abkowitz, Janis L.
Formato: Artigo
Idioma:Inglês
Publicado: American Society of Hematology 2020
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC7685213/
https://ncbi.nlm.nih.gov/pubmed/33211834
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/blood.2020007968
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