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Inducing iron deficiency improves erythropoiesis and photosensitivity in congenital erythropoietic porphyria

Congenital erythropoietic porphyria (CEP) is an autosomal recessive disorder of heme synthesis characterized by reduced activity of uroporphyrinogen III synthase and the accumulation of nonphysiologic isomer I porphyrin metabolites, resulting in ineffective erythropoiesis and devastating skin photos...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Argitaratua izan da:Blood
Egile Nagusiak: Egan, Daniel N., Yang, Zhantao, Phillips, John, Abkowitz, Janis L.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: American Society of Hematology 2015
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC4497965/
https://ncbi.nlm.nih.gov/pubmed/25972160
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/blood-2014-07-584664
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