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Inducing iron deficiency improves erythropoiesis and photosensitivity in congenital erythropoietic porphyria

Congenital erythropoietic porphyria (CEP) is an autosomal recessive disorder of heme synthesis characterized by reduced activity of uroporphyrinogen III synthase and the accumulation of nonphysiologic isomer I porphyrin metabolites, resulting in ineffective erythropoiesis and devastating skin photos...

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Dades bibliogràfiques
Publicat a:Blood
Autors principals: Egan, Daniel N., Yang, Zhantao, Phillips, John, Abkowitz, Janis L.
Format: Artigo
Idioma:Inglês
Publicat: American Society of Hematology 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4497965/
https://ncbi.nlm.nih.gov/pubmed/25972160
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1182/blood-2014-07-584664
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