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Biomarkers in Anderson–Fabry Disease

Fabry disease is a rare lysosomal storage disorder caused by a deficiency of α-galactosidase A, resulting in multisystemic involvement. Lyso-Gb3 (globotriaosylsphingosine), the deacylated form of Gb3, is currently measured in plasma as a biomarker of classic Fabry disease. Intensive research of biom...

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書目詳細資料
發表在:Int J Mol Sci
Main Authors: Simonetta, Irene, Tuttolomondo, Antonino, Daidone, Mario, Pinto, Antonio
格式: Artigo
語言:Inglês
出版: MDPI 2020
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在線閱讀:https://ncbi.nlm.nih.gov/pmc/articles/PMC7662984/
https://ncbi.nlm.nih.gov/pubmed/33138098
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms21218080
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