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Real-World Clinical Experience With Idebenone in the Treatment of Leber Hereditary Optic Neuropathy

BACKGROUND: Leber hereditary optic neuropathy (LHON) leads to bilateral central vision loss. In a clinical trial setting, idebenone has been shown to be safe and to provide a trend toward improved visual acuity, but long-term evidence of effectiveness in real-world clinical practice is sparse. METHO...

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Publicado en:J Neuroophthalmol
Autores principales: Catarino, Claudia B., von Livonius, Bettina, Priglinger, Claudia, Banik, Rudrani, Matloob, Selma, Tamhankar, Madhura A., Castillo, Lorena, Friedburg, Christoph, Halfpenny, Christopher A., Lincoln, John A., Traber, Ghislaine L., Acaroglu, Gölge, Black, Graeme C. M., Doncel, Carlos, Fraser, Clare L., Jakubaszko, Joanna, Landau, Klara, Langenegger, Stefan J., Muñoz-Negrete, Francisco J., Newman, Nancy J., Poulton, Joanna, Scoppettuolo, Elisabetta, Subramanian, Prem, Toosy, Ahmed T., Vidal, Mariona, Vincent, Andrea L., Votruba, Marcela, Zarowski, Marcin, Zermansky, Adam, Lob, Felice, Rudolph, Günther, Mikazans, Oskars, Silva, Magda, Llòria, Xavier, Metz, Günther, Klopstock, Thomas
Formato: Artigo
Lenguaje:Inglês
Publicado: Journal of Neuro-Ophthalmology 2020
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC7657145/
https://ncbi.nlm.nih.gov/pubmed/32991388
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1097/WNO.0000000000001023
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