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Animal Models of CMT2A: State-of-art and Therapeutic Implications

Charcot–Marie–Tooth disease type 2A (CMT2A), arising from mitofusin 2 (MFN2) gene mutations, is the most common inherited axonal neuropathy affecting motor and sensory neurons. The cellular and molecular mechanisms by which MFN2 mutations determine neuronal degeneration are largely unclear. No effec...

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Библиографические подробности
Опубликовано в: :Mol Neurobiol
Главные авторы: De Gioia, Roberta, Citterio, Gaia, Abati, Elena, Nizzardo, Monica, Bresolin, Nereo, Comi, Giacomo Pietro, Corti, Stefania, Rizzo, Federica
Формат: Artigo
Язык:Inglês
Опубликовано: Springer US 2020
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC7541381/
https://ncbi.nlm.nih.gov/pubmed/32856204
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s12035-020-02081-3
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