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Human iPSC-Based Models for the Development of Therapeutics Targeting Neurodegenerative Lysosomal Storage Diseases

Lysosomal storage diseases (LSDs) are a group of rare genetic conditions. The absence or deficiency of lysosomal proteins leads to excessive storage of undigested materials and drives secondary pathological mechanisms including autophagy, calcium homeostasis, ER stress, and mitochondrial abnormaliti...

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Publicat a:Front Mol Biosci
Autors principals: Luciani, Marco, Gritti, Angela, Meneghini, Vasco
Format: Artigo
Idioma:Inglês
Publicat: Frontiers Media S.A. 2020
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC7530250/
https://ncbi.nlm.nih.gov/pubmed/33062642
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3389/fmolb.2020.00224
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