Загрузка...

Gene Therapy for Hemophilia: Facts and Quandaries in the 21st Century

Therapy for hemophilia has evolved in the last 40 years from plasma-based concentrates to recombinant proteins and, more recently, to non-factor therapeutics. Along this same timeline, research in adeno-associated viral (AAV) based gene therapy vectors has provided the framework for early phase clin...

Полное описание

Сохранить в:
Библиографические подробности
Опубликовано в: :Mediterr J Hematol Infect Dis
Главные авторы: Arruda, Valder R., Doshi, Bhavya S.
Формат: Artigo
Язык:Inglês
Опубликовано: Università Cattolica del Sacro Cuore 2020
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC7485465/
https://ncbi.nlm.nih.gov/pubmed/32952980
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.4084/MJHID.2020.069
Метки: Добавить метку
Нет меток, Требуется 1-ая метка записи!