Загрузка...
Obstacles and future of gene therapy for hemophilia
INTRODUCTION: The recent success of early-phase clinical trials for adeno-associated viral (AAV) liver-directed gene therapy for hemophilia B (HB) demonstrates the potential for gene therapy, in the future, to succeed protein-based prophylaxis therapy for HB. Significant obstacles, however, need to...
Сохранить в:
| Опубликовано в: : | Expert Opin Orphan Drugs |
|---|---|
| Главные авторы: | , |
| Формат: | Artigo |
| Язык: | Inglês |
| Опубликовано: |
2015
|
| Предметы: | |
| Online-ссылка: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4756761/ https://ncbi.nlm.nih.gov/pubmed/26900534 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1517/21678707.2015.1069179 |
| Метки: |
Добавить метку
Нет меток, Требуется 1-ая метка записи!
|