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Clinical Efficacy Evaluation of Sirolimus in Congenital Hyperinsulinism
BACKGROUND: Congenital hyperinsulinism (CHI) is a rare and life-threatening genetic disorder. Sirolimus as a mammalian target of rapamycin inhibitor may be helpful in patients with CHI who do not respond well to other treatments including diazoxide and octreotide. However, the safety and efficacy of...
Gorde:
| Argitaratua izan da: | Int J Endocrinol |
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| Egile Nagusiak: | , , , , , |
| Formatua: | Artigo |
| Hizkuntza: | Inglês |
| Argitaratua: |
Hindawi
2020
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| Gaiak: | |
| Sarrera elektronikoa: | https://ncbi.nlm.nih.gov/pmc/articles/PMC7396056/ https://ncbi.nlm.nih.gov/pubmed/32774365 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1155/2020/7250406 |
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