Caricamento...

Nonsense Suppression Therapy: New Hypothesis for the Treatment of Inherited Bone Marrow Failure Syndromes

Inherited bone marrow failure syndromes (IBMFS) are a group of cancer-prone genetic diseases characterized by hypocellular bone marrow with impairment in one or more hematopoietic lineages. The pathogenesis of IBMFS involves mutations in several genes which encode for proteins involved in DNA repair...

Descrizione completa

Salvato in:
Dettagli Bibliografici
Pubblicato in:Int J Mol Sci
Autori principali: Bezzerri, Valentino, Api, Martina, Allegri, Marisole, Fabrizzi, Benedetta, Corey, Seth J., Cipolli, Marco
Natura: Artigo
Lingua:Inglês
Pubblicazione: MDPI 2020
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7369780/
https://ncbi.nlm.nih.gov/pubmed/32630050
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/ijms21134672
Tags: Aggiungi Tag
Nessun Tag, puoi essere il primo ad aggiungerne! !