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BEON: A Functional Fluorescence Reporter for Quantification and Enrichment of Adenine Base-Editing Activity

Adenine base editor (ABE) is a new generation of genome-editing technology through fusion of Cas9 nickase with an evolved E. coli TadA (TadA∗) and holds great promise as novel genome-editing therapeutics for treating genetic disorders. ABEs can directly convert A-T to G-C in specific genomic DNA tar...

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Pubblicato in:Mol Ther
Autori principali: Wang, Peipei, Xu, Li, Gao, Yandi, Han, Renzhi
Natura: Artigo
Lingua:Inglês
Pubblicazione: American Society of Gene & Cell Therapy 2020
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC7335737/
https://ncbi.nlm.nih.gov/pubmed/32353322
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ymthe.2020.04.009
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