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Mapping RNA splicing variations in clinically-accessible and non-accessible tissues to facilitate Mendelian disease diagnosis using RNA-seq

PURPOSE: RNA-seq is a promising approach to improve diagnoses by detecting pathogenic aberrations in RNA splicing that are missed by DNA sequencing. RNA-seq is typically performed on clinically-accessible tissues (CATs) from blood and skin. RNA tissue-specificity makes it difficult to identify aberr...

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Bibliographic Details
Published in:Genet Med
Main Authors: Aicher, Joseph K, Jewell, Paul, Vaquero-Garcia, Jorge, Barash, Yoseph, Bhoj, Elizabeth J
Format: Artigo
Language:Inglês
Published: 2020
Subjects:
Online Access:https://ncbi.nlm.nih.gov/pmc/articles/PMC7335339/
https://ncbi.nlm.nih.gov/pubmed/32225167
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/s41436-020-0780-y
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